Sign In
Cook Children's
Patient Portal

Active Research Projects

Research icon

Our research team is always looking for ways to improve the health of children. There are several clinical trials that are currently under way.

For questions on our research operations, please contact Dennis Carson at 682-885-7491.

What type of research study are you looking for?

Research study listing:

Project TitlePrinciple Investigator
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs) for Transplantation in Pediatric and Adult Patients with Hematologic Malignancies and Other IndicationsEames
The Use of Fluorodopa 18F Positron Emission Tomography Combined with Computed Tomography in Congenital HyperinsulinismThornton
Safety Attitude Questionnaire
Vagus Nerve Stimulator Placement in the Pediatric Patient
Diagnoses and outcomes in temporal lobectomies in children: assessing the utilityof iMRI and en bloc hippocampal resection
Perceived Understanding, Use, and Importance of Genetic and Genomic Competencies by Pediatric Nurses
The Occurrence and Distribution of Second Malignancy Following Initial Diagnosis and Treatment of Childhood Cancer at Cook Children's Medical Center: Implications for Survivorship and Long-term Follow-up
The Prevalence and Incidence of Patients with Non-Epileptic Seizures and Duration of Epileptic Seizures in the EMU
Front Line Nurses Experiences in Caring for Pediatric Patients & Families with Limited English Proficiency
Hypothermia in Pre-Term Infants
The Influence of Hypothermia on the Outcome of Premature Birth
Cardiometabolic Risk (C.M.R.) Research Registry
Structural Equation Models of Necrotizing Enterocolitis
A motivational and family-based weight management program (FIT for Health Fort Worth)
Electroencephalographic characteristics of status epilepticus in cat scratch disease encephalopathy
Sample size in length of stay studies
Post-Surgical Neuropsychological Outcomes in Pediatric Patients Undergoing Temporal Lobe Epilepsy Surgery
Study of Obesity in Survivors of Childhood Acute Lymphoblastic Leukemia (ALL)
Developmental Trajectories and Predictors of Health Outcomes in Normal and Low Birth Weight Individuals
Trends in Health Problems and Care in Normal and Low Birth Weight Children and Teenagers-Part A
Outcomes Following Treatment for Modern Osteosarcoma: The Cook Children's Experience
Survey of the National Lipid Association’s Membership - Opinions of the 2011 National Heart, Lung and Blood Institute’s Expert Panel Guidelines for Cardiovascular Health and Risk Reduction in Children and Adolescents.
Therapeutic Leukapheresis in Management of Hyperleukocytosis in Children, A Single Institution Experience.
Cook Children’s Nurses Knowledge and Readiness to Use Evidence Based Practice: A 6 Year Follow-up Study
Classification of Children with Newly Diagnosed Diabetes Mellitus
Reproductive Health in Female Members of Cook Children's Life After Cancer Program
A Process Improvement Tool to Enhance and Monitor the Treatment of Children and Adolescents with Diabetic Ketoacidosis (DKA)
Analysis of duration of stay and number of seizures necessary to achieve accurate localization of the epileptogenic zone using video EEG monitoring data in pediatric patients
Care of Children with Diabetic Ketoacidosis in Hospital Emergency Departments
Examine The Influence Of A Cancer Diagnosis And Treatment On The Educational And Career Path In Adolescents And Young Adult Survivors Of Cancer Diagnosed During Adolescence: A Single Institution ExperienceBashore
Impact of coregistered multimodal neuroimaging on pediatric epilepsy surgery planning and postoperative outcome
An Open-Label Trial of Triheptanoin in Patients with Glucose Transporter Type-1 Deficiency Syndrome (GLUT1 DS)Lacy
Hematopoietic Stem Cell Transplantation in Pediatric Sickle Cell Disease: The Cook Children's Experience
Neuropsychological Outcomes of Patients with Jeavons Syndrome
An Evaluation of the Utilization of Whole Exome Sequencing as a Diagnostic Tool in Patients with Neurological Diseases
Establishment of the Pediatric Obesity Weight Evaluation Registry (POWER): A Prospective Pilot Project of Children and Adolescents Presenting for Weight Management
Clinicopathological Correlation Of Pediatric Gonadectomies For Neoplastic And Non-Neoplastic Conditions, A 13 Year Experience At A Single Institution
Identification Of A Clinicopathological Correlation Between Prevalence Of Testicular Torsion And Temperature In Adolescent Males Between Ten And Eighteen Years Of Age In The North Texas Climate
COG AALL05B1: A Children's Oncology Group Protocol for Collecting and Banking Relapsed Acute Lymphoblastic Leukemia Research SpecimensHeym
Classification Of Newly Diagnosed Acute Lymphoblastic LeukemiaHeym
Treatment Of Patients With Newly Diagnosed Standard Risk B-Precursor Acute Lymphoblastic Leukemia (All)Heym
A Phase III Randomized Trial For Newly Diagnosed High Risk B-Lymphoblastic Leukemia (B-ALL) Testing Clofarabine (IND# 73789, NSC# 606869) in the Very High Risk StratumHeym
A Phase III Randomized Trial Investigating Bortezomib (NSC# 681239; IND# 58443) on a Modified Augmented BFM (ABFM) Backbone in Newly Diagnosed T-Lymphoblastic Leukemia (T-ALL) and T-Lymphoblastic Lymphoma (T-LLy)Heym
Risk-Stratified Randomized Phase III Testing of Blinatumomab (IND# 117467, NSC#765986) in First Relapse of Childhood B-Lymphoblastic Leukemia (B-ALL)Heym
Biology Study Of Transient Myeloproliferative Disorder (Tmd) In Children With Down Syndrome (DS)Heym
A Phase III Randomized Trial for Patients with De Novo AML Using Bortezomib (IND# 58443, NSC# 681239) and Sorafenib (BAY 43-9006, IND#69896, NSC# 724772) for Patients with High Allelic Ratio FLT3/ITDHeym
A Phase III Study for Patients with Newly Diagnosed Acute Promyelocytic Leukemia (APL) using Arsenic Trioxide and All-Trans Retinoic AcidHeym
AAML1531, Risk-stratified Therapy for Acute Myeloid Leukemia in Down SyndromeHeym
A Children's Oncology Group Protocol For Collecting And Banking Pediatric Research SpecimensAkers
A Comprehensive Approach to Improve Medication Adherence in Pediatric ALLAlbritton
Impact of Cleansing with Chlorhexidine Gluconate (CHG) on Reducing Central Line Associated Bloodstream Infection (CLABSI) and Acquisition of Multi-drug Resistant Organisms (MDRO) in Children with Cancer or Those Receiving Allogeneic Hematopoietic Cell Transplantation (HCT)Granger
Protocol For The Enrollment On The Official Cog Registry, The Childhood Cancer Research Network (Ccrn)Granger
A Children's Oncology Group Protocol For Collecting And Banking Pediatric Brain Tumor Research SpecimensMurray
Efficacy Of Carboplatin Administered Concomitantly With Radiation And Isotretinoin As A Pro-Apoptotic Agent In Other Than Average Risk Medulloblastoma/Pnet PatientsMurray
Phase III Randomized Trial of Post-Radiation Chemotherapy in Patients with Newly Diagnosed Ependymoma Ages 1 to 21 yearsMurray
Activa® Dystonia TherapyMarks
A Phase II Trial of Pazopanib (GW786034, NSC# 737754) in Children, Adolescents and Young Adults with Refractory Solid TumorsAlbritton
A COG Study For Collecting And Banking Ewing Sarcoma SpecimensAkers
AHEP0731: Treatment of Children with All Stages of Hepatoblastoma with Temsirolimus (IND# 122782, NSC# 683864) Added to High Risk Stratum TreatmentAkers
A Randomized Phase III Study of Brentuximab Vedotin (SGN-35, IND #117117) for Newly Diagnosed High-Risk Classical Hodgkin Lymphoma (cHL) in Children and AdolescentsHeym
Abobott AL16: Comparison of Two Human Milk Fortifiers in Preterm InfantsRiley
Phase 3, Randomized, Double-Blind, Active-Controlled Study of ALXN1210 Versus Eculizumab in Complement Inhibitor-Naïve Adult Patients with Paroxysmal Nocturnal Hemoglobinuria (PNH)Beam
A Phase II Study of Therapy for Pediatric Relapsed or Refractory Pre-cursor B-cell Acute Lymphoblastic Leukemia and LymphomaHeym
ALTE03N1 - Key Adverse Events After Childhood CancerGranger
Long-Term Follow-Up of Patients Who Have Participated in Children's Oncology Group StudiesGranger
ALTE07C1, Neuropsychological, Social, Emotional, and Behavioral Outcomes in Children with CancerGranger
Longitudinal Assessment of Ovarian Reserve in Adolescents with LymphomaAlbritton
Health Effects after Anthracycline and Radiation Therapy (HEART): Dexrazoxane and Prevention of Anthracycline-related CardiomyopathyBeam
AML08, A Phase III Randomized Trial of Clofarabine Plus Cytarabine versus Conventional Induction Therapy and a Phase II Study of Natural Killer Cell Transplantation in Patients with Newly Diagnosed Acute Myeloid Leukemia
Neuroblastoma Biology StudiesGranger
A Phase II Randomized Trial of Irinotecan/Temozolomide with Temsirolimus (NSC# 683864, IND# 61010) or Chimeric 14.18 Antibody (ch14.18) (NSC# 764038, IND# 4308) in Children with Refractory, Relapsed or Progressive NeuroblastomaGranger
Utilizing Response- and Biology-Based Risk Factors to Guide Therapy in Patients with Non-High- Risk NeuroblastomaGranger
ANHL12P1, A Randomized Phase II Trial of Brentuximab Vedotin or Crizotinib in combination with Chemotherapy for Newly Diagnosed Patients with ALCL (IND#117117)Heym
A Children's Oncology Group Protocol for Collecting and Banking Osteosarcoma SpecimensAkers
Phase 2 Study of Denosumab (IND# 127430, NSC# 744010), a RANK Ligand Antibody, for Recurrent or Refractory OsteosarcomaAkers
Renal Tumors Classification, Biology, and Banking StudyVallance
Pazopanib Neoadjuvant Trial in Non-Rhabdomyosarcoma Soft Tissue Sarcomas (PAZNTIS): A Phase II/III Randomized Trial of Preoperative Chemoradiation or Preoperative Radiation Plus or Minus Pazopanib (NSC# 737754, IND# 118613)Albritton
TransCon hGH CT-301, A multicenter, Phase 3, randomized, open-label, active-controlled, parallel-group trial investigating the safety, tolerability, and efficacy of TransCon hGH administered once a week versus standard daily hGH replacement therapy over 52 weeks in prepubertal children with growth hormone deficiency (GHD)Thornton
A Phase 3, Multicenter, Investigator-blind, Randomized, Parallel Group Study to Investigate the Safety and Efficacy of Fidaxomicin Oral Suspension or Tablets Taken q12h, and Vancomycin Oral Liquid or Capsules Taken q6h, for 10 Days in Pediatric Subjects With Clostridium Difficile-associated DiarrheaMazade
ATHN RegistrySanders
Gemtuzumab Ozogamicin (Mylotarg®) Expanded Access Protocol for Treatment of Patients in the United States with Relapsed/Refractory Acute Myelogenous Leukemia Who May Benefit From Treatment and Have No Access to Other Comparable/Alternative TherapyAkers
BAY 59-7939/14372, Multicentre, open-label, active-controlled, randomized study to evaluate the efficacy and safety of an age- and body weight-adjusted rivaroxaban regimen in children with acute venous thromboembolismTorres
A Long-Term Non-Interventional Registry to Assess Safety and Effectiveness of Humira® (Adalimumab) in Pediatric Patients with Moderately to Severely Active Crohn's Disease (CD).Ogunmola
Comparison Between Surgical versus Balloon Angioplasty versus Intravascular Stent Placement for Recurrent or Native Coarctation of the AortaSchutte
Expanded Access Use of Omegaven® in the Treatment of Parenteral Nutrition Induced Liver Injury in ChildrenOsuntokun
CCSS Childhood Cancer Survivor StudyBowman
CDC Public Health Surveillance for Bleeding Disorders- Registry for Bleeding Disorders SurveillanceSanders
A Phase 2, Multicenter, Randomized, Double-blind, Placebo-controlled, Parallel Group Study to Evaluate the Efficacy, Safety, and Tolerability of CTX-4430 Administered Orally Once-Daily for 48 Weeks in Patients with Cystic FibrosisSchultz
A Long-term Prospective Observational Safety Study of the Incidence of and Risk Factors for Fibrosing Colonopathy in US Patients with Cystic Fibrosis Treated with Pancreatic Enzyme Replacement Therapy: A Harmonized Protocol across SponsorsCunningham
–“ An Intermediate-size, Expanded Access Protocol to Provide Brincidofovir for the Treatment of Serious Adenovirus Infection or Disease”Howrey
Clinical Validation of a Short Screening Tool for Identifying Victims of Child Sex Trafficking And Commercial Sexual Exploitation in the Health Care Setting
A point prevalence survey regarding antibiotic use in children for four two week blocks.Mazade
ALTE1621, Pharmacologic Reversal of Ventricular Remodeling in Childhood Cancer Survivors at Risk for Heart Failure (PReVent-HF): A Phase 2b Randomized Placebo-Controlled (Carvedilol) TrialBeam
Comprehensive Epilepsy Center Surgical Database ProjectPerry
A Randomized, Blinded, Single Institution Evaluation of Topical Tobramycin/Dexamethasone vs. Eyelid Hygiene in the Treatment of Blepharitis in a Pediatric Population
Participation in the Cystic Fibrosis Patient RegistryCunningham
A COG Soft Tissue Sarcoma Diagnosis, Biology and Banking ProtocolAkers
Parental Decision-Making for Children with Relapsed NeuroblastomaGranger
PROTOCOL 03-CL-1202: A MULTINATIONAL, MULTICENTER, MASKED, RANDOMIZED, CONTROLLED STUDY TO ASSESS THE SAFETY AND EFFICACY OF LUCINACTANT FOR INHALATION IN PRETERM NEONATES 26 TO 32 WEEKS GESTATIONAL AGE WITH RESPIRATORY DISTRESS SYNDROMERiley
Encephalitis Chart Review
The EPIC Observational Study: Longitudinal Assessment of Risk-Factors For and Impact of Pseudomonas Aeruginosa Acquisition and Early Anti-Pseudomonal Treatment in Children with CFDyson
Frequency of Targetable Genomic Alterations in NeuroblastomaGranger
Pilot Study of the Genetic Epidemiology of Childhood CancerBowman
LSD RegistryGillespie
A Randomized, Double-Blind Evaluation of the Pharmacokinetics, Safety, and Antiviral Efficacy of Tenofovir Alafenamide (TAF) in Adolescents with Chronic Hepatitis B Virus InfectionWhitworth
A Long Term Follow-up Registry for Adolescent and Pediatric Subjects Who Received a Gilead Hepatitis C Virus Direct Acting Antiviral (DAA) in Gilead-Sponsored Chronic Hepatitis C Infection TrialsWhitworth
A Phase 2, Open-Label, Multicenter, Multi-cohort Study to Investigate the Safety and Efficacy of Ledipasvir/Sofosbuvir Fixed Dose Combination in Adolescents and Children with Chronic HCV-InfectionWhitworth
An open label extension study to investigate the safety of cannabidiol (GWP42003-P; CBD) in children and adults with inadequately controlled Dravet or Lennox-Gastaut SyndromesPerry
A Randomized, Double-Blind, Placebo-Controlled Study to Investigate the Efficacy and Safety of Cannabidiol(GWP42003-P) in Children and Young Adults with Dravet Syndrome. GWEP1424 GWEP1424Perry
H6650, Texas Children's Cancer Center and Hematology Service Tissue BankMurray
Multi Center iMRI Neurosurgery DatabaseHoneycutt
Improve Care NowOgunmola
Outcomes in Term and Late Pre-Term Infants with Congenital Heart DefectsNedrelow
Towards the Establishment of Standards of Practice and the Inititation of Multi-Center, Multi-National Clinical Trials for Neonates and Children with StrokeTorres
Isocyanate Exposure in Neonatal Infants in the Neonatal Intensive Care Unit (NICU) at Cook Children's Medical CenterNedrelow
A Phase 4, Multicenter, Open-label Study of Serum Infliximab Concentrations and Efficacy and Safety of Dose Escalation in Pediatric Patients with Inflammatory Bowel DiseaseOgunmola
A Multicenter, Prospective, Long-term, Observational Registry of Pediatric Patients with Inflammatory Bowel Disease.Ogunmola
A Phase 3, Randomized, Adaptive Study Comparing the Efficacy and Safety of Defibrotide vs Best Supportive Care in the Prevention of Hepatic Veno-Occlusive Disease in Adult and Pediatric Patients Undergoing Hematopoietic Stem Cell TransplantGranger
“Preservation of Thoracic Kyphosis and Coronal Curve Correction as a Function of Rod Stiffness in the Surgical Treatment of Adolescent Idiopathic Scoliosis with the Use of the K2M MESA Rail™ Deformity System”Gray
A Study to Identify the Frequency of Lysosomal Acid Lipase Deficiency in at-risk Patient PopulationsWilson
Pediatric Submersion Injury
Pediatric Use for Liposorber Apheresis SystemGillespie
Management of mediastinal masses: a quality improvement and research initiative
ACCESS DMD™, an expanded access program that is now available for children, adolescents, and adults in the U.S. diagnosed with Duchenne muscular dystrophy (DMD)Marks
Patent Ductus Arteriosus Post NICU Discharge in Premature Infants: A Prospective RegistryRiley
An Open-Label, Expanded Access Protocol Using 131-I-Metaiodobenzylguanidine (131 I-MIBG) Therapy in Patients with Refractory Neuroblastoma, Pheochromocytoma, or ParagangliomaGranger
Molecularly Targeted Therapy for Soft Tissue Sarcoma in Texas Biospecimen Banking ProtocolAlbritton
A Phase III Multicenter, Double-Blind, Randomized, Placebo-Controlled Clinical Trial to Evaluate the Safety and Efficacy of MK-0431A XR (a Fixed-Dose Combination Tablet of Sitagliptin and Extended-Release Metformin) in Pediatric Subjects with Type 2 Diabetes Mellitus With Inadequate Glycemic Control on Metformin Monotherapy.Wilson
A Phase I/II Study of Pembrolizumab (MK-3475) in Children with advanced melanoma or a PD-L1 positive advanced, relapsed or refractory solid tumor or lymphoma (KEYNOTE-051)Granger
My Life Our Future: A Hemophilia Genotyping Initiative Data and Sample Research RepositorySanders
Neuroblastoma Biology Study, NANTGranger
RANDOMIZED PHASE II STUDY OF 131I-MIBG VS. 131I-MIBG WITH VINCRISTINE AND IRINOTECAN VS. 131I-MIBG WITH VORINOSTAT FOR RESISTANT/RELAPSED NEUROBLASTOMAGranger
A Phase I Study of Lenalidomide and Anti-GD2 Mab Ch14.18+/-Isotretinoin in Patients with Refractory/Recurrent NeuroblastomaGranger
A Long Term Follow-Up Umbrella Protocol to Cover NANT Studies to Allow the Collection of Long Term Follow-Up DataGranger
A Phase I Study of Difluoromethylornithine (DFMO) and Celecoxib with Cyclophosphamide/Topotecan for Patients with Relapsed or Refractory NeuroblastomaGranger
A Phase I Study of Sorafenib and Topotecan and Cyclophosphamide in Patients with Refractory/Recurrent/Persistent NeuroblastomaGranger
NANT2015-01 Precision Trial ProtocolGranger
An Exploratory Study of Voicing My CHOiCES™ as a Tool for Advanced Care Planning in Young Adults with Cancer and Other Life Threatening IllnessesHeath,
Infantile Spasms Multicenter DatabaseKeator
Blood Collection for National Marrow Donor ProgramEames
Protocol for a Research Database for Hematopoietic Stem Cell Transplantation and Marrow Toxic InjuriesEames
Efficacy and safety of liraglutide in combination with metformin versus metformin monotherapy on glycemic control in children and adolescents with type 2 diabetes A 26-week double-blind, randomized, parallel group, placebo controlled multi-center trial followed by a 26-week open-label extensionWilson
A multicenter safety study of unlicensed, investigational, cryopreserved cord blood units (CBUs) manufactured by the National Cord Blood Program (“NCBP”) and provided for unrelated hematopoietic stem cell transplantation of pediatric and adult patientsEames
PANAML: A Phase I and Dose Expansion Cohort Study of Panobinostat In Combination With Fludarabine And Cytarabine In Pediatric Patients With Refractory Or Relapsed Acute Myeloid Leukemia or Myelodysplastic SyndromeHeym
A Retrospective Chart Analysis of Survival Rate and Treatment-related Mortality Following Post Myeloablative Stem Cell/Bone Marrow Transplant in Pediatric Acute Lymphoblastic LeukemiaBowman
Patient Care Evaluation Study of Institutional Kidney TumorsVallance
Validation of the English and Spanish Versions of the PedsQL 3.2 Diabetes Module Background and Rationale
National Validation of the PedsQL-Epilepsy ModulePerry
A Phase 3, Multicenter, Randomized, Double Blind, Placebo Controlled, Parallel Group Study to Evaluate the Efficacy and Safety of Rivipansel (GMI 1070) in the Treatment of Vaso Occlusive Crisis in Hospitalized Subjects With Sickle Cell DiseaseJohnson
Pediatric Intravenous versus Oral Antibiotic Therapy (PIVVOT) StudyMazade
Establishment of the Pediatric Obesity Weight Evaluation Registry (POWER): A prospective pilot project of children and adolescents presenting for weight management.de
THE PROJECT EVERYCHILD PROTOCOL: A REGISTRY, ELIGIBILITY SCREENING, BIOLOGY AND OUTCOME STUDYGranger
A Randomized Trial of the Use of Human Milk Cream to Decrease Length of Stay in Extremely Premature InfantsRiley
Reduced Burden of Oncologic Therapy in Advanced B-cell Lymphoma (REBOOT ABLY) in Children, Adolescents and Young Adults with CD20+ Mature B-Cell LymphomaHeym
Remodulin in Neonatal PPHNRiley
RISK ADAPTED FOCAL PROTON BEAM RADIATION AND/OR SURGERY IN PARTICIPANTS WITH LOW, INTERMEDIATE AND HIGH RISK RHABDOMYOSARCOMA RECEIVING STANDARD OR INTENSIFIED CHEMOTHERAPYAlbritton
A Multicentre, Long-term Safety, Efficacy, and Pharmacokinetics Study of Lubiprostone in Paediatric Subjects Aged = 6 Years to < 18 Years with Functional Constipation (Extension Study)Osuntokun
AN OPEN LABEL, EXPANDED ACCESS PROTOCOL TO EVALUATE THE EFFICACY AND SAFETY OF SAGE-547 INJECTION IN THE TREATMENT OF SUBJECTS WITH SUPER-REFRACTORY STATUS EPILEPTICUS
A Phase III Double-blind, Randomized, Placebo-Controlled Study assessing the Efficacy, Safety and Tolerability of Idebenone in Patients with Duchenne Muscular Dystrophy Receiving Glucocorticoid steroidsMarks
International Registry for Severe Chronic NeutropeniaBeam
A Clinical and Molecular Risk-Detected Therapy for Newly Diagnosed Medulloblastoma (SJMB12)Heym
Phase I Study of Fenretinide (4-HPR, NSC 374551) Lym-X-Sorb?(LXS) Oral Powder Plus Ketoconazole Plus Vincristine in Patients with Recurrent or Resistant Neuroblastoma (IND #: 68,254)Granger
Expanded Access Study of Fenretinide (4-HPR, NSC 374551) Lym-X-Sorb?(LXS) Oral Powder Plus Ketoconazole in Patients with Recurrent or Resistant Neuroblastoma (IND #68,254)Granger
Expanded Access Use of Stiripentol in Participants with Dravet Syndrome or Epileptic Encephalopathies Associated with SCN1A MutationsPerry
A Pilot Study of Vincristine Sulfate Liposome Injection (Marqibo®) in Combination with UK ALL R3 Induction Chemotherapy for Children, Adolescents, and Young Adults with Relapse of Acute Lymphoblastic Leukemia
T2014-001, A Phase I Trial of Temsirolimus (CCI-779, Pfizer, Inc.) in Combination with Etoposide and Cyclophosphamide in Children with Relapsed Acute Lymphoblastic Leukemia and Non-Hodgkins LymphomaHeym
Protocol for Collecting, Banking and Distrbuting Human Tissue SamplesHeym
A MULTICENTER RETROSPECTIVE REVIEW OF PEDIATRIC MELANOMAHeym
Test ProtocolAkers
Clinical Assessment of Flow in Tetralogy of Fallot by Time-Resolved Volumetric Phase Contrast MRIMuyskens
TOPNOC 001-08, A Phase 2 Study of Valproic Acid and Radiation, followed by Maintenance Valproic Acid and Bevacizumab in Children with Newly Diagnosed High-Grade Gliomas or Brainstem GliomasMurray
CASE ASCERTAINMENT FOR EPIDEMIOLOGIC STUDIES OF CHILDHOOD CANCERSMurray
Case Ascertainment for Epidemiologic Studies of Childhood Cancers (Molecular Characterization of Pediatric Brain Tumors)Murray
TR701-122 - Phase 3 Study of IV to Oral 6-Day Tedizolid Phosphate Compared with 10-Day Comparator in Subjects 12 to <18 Years with cSSTIRios
Molecular characterization of immune receptors and gene-specific hypermethylation in Hispanic, Caucasian and African American children with Acute Lymphoblastic Leukemia (ALL).Mathew
A Randomized, Double-Blind, Placebo-Controlled, Parallel-Group, Adaptive Study to Assess the Safety and Efficacy of UX007 in Subjects with Glucose Transporter Type 1 Deficiency SyndromeLacy
An Open-label Study to Assess the Long-term Safety and Efficacy of UX007 in Subjects with Glucose Transporter Type 1 Deficiency Syndrome” to be conducted pursuant to Protocol UX007G-CL202Lacy
A Phase 2a, Randomized, Double blind, Placebo controlled, Incomplete Block, Crossover Study to Evaluate the Safety and Efficacy of VX-371 in Subjects Aged 12 Years or Older With Cystic Fibrosis, Homozygous for the F508del CFTR Mutation, and Being Treated With Orkambi.Schultz
an extension of VAX14-661-106Schultz
A Phase 2, Four-part, Randomized, Double-blind, Placebo- and VX-661/ivacaftor-controlled, Parallel Arm, Multicenter Study to Evaluate the Safety, Pharmacokinetics, Pharmacodynamics, and Efficacy of VX-152 Monotherapy and VX-152 in Dual and Triple Combination With VX-661 and Ivacaftor in Subjects Aged 12 Years and Older With Cystic FibrosisSchultz
PEDIATRIC DELIRIUM: A MULTI-INSTITUTIONAL POINT PREVALENCE STUDY
PROTOCOL XSGO-CHO1, A PHASE 2 PROOF-OF-CONCEPT STUDY OF CSIGLUCAGON ™ (CONTINUOUS SUBCUTANEOUS GLUCAGON INFUSION) TO PREVENT HYPOGLYCEMIA WITH LOWER INTRAVENOUS GLUCOSE INFUSION RATES IN CHILDREN UP TO ONE YEAR OF AGE WITH CONGENITAL HYPERINSULINISMThornton
ZX008-1501, A Multicenter, Randomized, Double-blind, Parallel Group, Placebo- controlled Trial of Two Fixed Doses of ZX008 (Fenfluramine Hydrochloride) Oral Solution as an Adjunctive Therapy in Children and Young Adults with Dravet SyndromePerry